Category: Severe Combined Immunodeficiency
New Gene Therapy Helps Those With “Bubble Boy” Disease
January 4th, 2023A new gene therapy is helping children with a rare form of “Bubble boy” disease live normal lives. Experts said the findings are a major advance for children with the disease –a subtype of severe combined immunodeficiency (SCID).
New Therapy Offers Ho… more »
Researchers Might Have Found a Cure for “Bubble Boy Disease”
May 1st, 2019Researchers believe they may have found a cure for x-linked severe combined immunodeficiency (SCID-X1), more commonly known as “Bubble Boy Disease.”
A Cure for SCID-X1
Researchers developed an experimental gene therapy that involves harvesting bone ma… more »